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Nationwide survey on the use of horse antithymocyte globulins (ATGAM) in patients with acquired aplastic anemia: A report on behalf of the French Reference Center for Aplastic Anemia. Peffault de Latour R et al. Am J Hematol. 2018 May.
A landscape of germ line mutations in a cohort of inherited bone marrow failure patients. Bluteau O et al. Blood. 2018 Feb 15.
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Avancée majeure dans le traitement de patientes enceintes atteintes d’Hémoglobinurie Paroxystique Nocturne (HPN): Eculizumab in Pregnant Patients with Paroxysmal Nocturnal Hemoglobinuria, N Engl J Med 2015; 373:1032-1039September 10, 2015
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Outcome of aplastic anaemia in children. A study by the severe aplastic anaemia and paediatric disease working parties of the European group blood and bone marrow transplant. Dufour C et al. British Journal of Haematology, 14 FEB 2015.
HLA-matched related-donor HSCT in Fanconi anemia patients conditioned with cyclophosphamide and fludarabine. Benajiba L et al. Blood 2015 125: 417-418.
Assessing complement blockade in patients with paroxysmal nocturnal hemoglobinuria receiving eculizumab. Peffault de Latour et al. Blood 2015; 125(5):775-783.
Paroxysmal nocturnal hemoglobinuria and hematopoietic stem cell transplantation: Better results in 2015? Sicre de Fontbrune et al. Leukemia & Lymphoma Volume 57, Issue 4, 2016.
Second allogeneic stem cell transplant for aplastic anaemia: a retrospective study by the Severe Aplastic Anaemia Working Party of the European Society for Blood and Marrow Transplantation. Cesaro S et al. British Journal of Haematology Volume 171, Issue 4, pages 606–614, November 2015.
Similar outcome of upfront-unrelated and matched sibling stem cell transplantation in idiopathic paediatric aplastic anaemia. A study on behalf of the UK Paediatric BMT Working Party, Paediatric Diseases Working Party and Severe Aplastic Anaemia Working Party of EBMT. Dufour C et al. British Journal of Haematology Volume 171, Issue 4, pages 585–594, November 2015.
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